The Promise and Perils of Next-Gen AAV Capsids
Our Science
Our Goals
Our Goal
Emugen's mission is to advance therapeutic strategies that target the root causes of complex neurological disorders. By harnessing the power of next-gen AAV capsids, we are developing innovative solutions to enable more precise, reliable, and scalable genetic treatments and ultimately, improving outcomes for patients with high unmet medical need.
Why Rett Syndrome?
platform
Regulated Gene Augmentation with Erase & Replace
Why Dravet Syndrome?
platform
Targeting Poison Exons to Address
Haploinsufficiency
PLATform
Next-Gen Splice Modulator
Our platform provides precise control over gene expression—enabling upregulation, downregulation, or complete gene replacement to achieve targeted therapeutic outcomes. It is designed for high specificity with minimal risk of off-target effects
PLATform
Circuit Modulation
Advanced AAV gene therapy enabling drug-controllable and titratable restoration of brain activity in neural circuits.
Our Programs
gene replacement
Introduction of functional genes to restore normal cellular function in affected cells.
Gene regulation
Precise control of gene expression through advanced regulatory elements, ensuring optimal therapeutic outcomes.
